Preclinical data show the vectorized miRNA candidate achieved durable knockdown of SCN9A (Na V 1.7), a genetically validated pain target historically difficult to modulate In non-human primates, ...
To date, ETX101 has shown a favorable safety profile and has been well-tolerated across all four dose levels with no treatment-related serious adverse events (n=19). The most common treatment-related ...
Information can be encoded into all sorts of patterns, whether it’s short and long beeps for Morse code, raised bumps for Braille, or ones and zeroes for computers. Now researchers have demonstrated a ...
DNA-encoded chemical library technologies are increasingly being adopted in drug discovery for hit and lead generation. DNA-encoded chemistry enables the exploration of chemical spaces four to five ...
Encoded Therapeutics to Present Interim Phase 1/2 Clinical Data on ETX101, the First One-time Gene Therapy in Development for Dravet Syndrome, at the 2025 American Epilepsy Society Annual Meeting – ...
University of Washington researcher Lee Organick (foreground) and Microsoft researcher Yuan-Jyue Chen (background) work in the Molecular Information Systems Lab. (UW Photo / Dennis Wise) Scientists ...
Suchi Rudra is a writer whose work has appeared in The New York Times, BBC, and Vice, among other publications. Storing digital data in RNA? It sounds like science fiction, but it’s not. Researchers ...
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