Sarepta's Duchenne gene therapy slows disease progression at three years

By Mariam Sunny Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for Duchenne muscular dystrophy slowed disease ...
KSDK

'You won't be alone': Families unite at Forest Park for MDA Muscle Walk

ST. LOUIS — On a cloudy morning in Forest Park, families gathered not just to take steps together but to take them for each other. The Muscular Dystrophy Association's 2025 Muscle Walk on May 4 drew ...
MedCity News

FDA Approves Sarepta Gene Therapy, But Only After Top FDA Official Bucks Agency Staff

A Sarepta Therapeutics gene therapy that failed its confirmatory test has now converted its accelerated FDA approval into a traditional one, expanding use of the treatment to a wider group of Duchenne ...
Manistee News Advocate on MSN

AMISH KITCHEN: Daughter Verena discusses her disability

"Muscular dystrophy can take many things from me, but it will not take away my happiness, nor will it take away my faith." ...
Boston Herald

Second patient death reported with gene therapy for muscular dystrophy

WASHINGTON (AP) — Shares of Sarepta Therapeutics plunged Monday after the biotech drugmaker reported a second death in connection with its gene therapy for muscular dystrophy. Sarepta reported the ...